Plasma proteome profiling combined with clinical and genetic features reveals the pathophysiological characteristics of β-thalassemia - ScienceDirect
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Β-Thalassemias | NEJM
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
PDF] Current and future alternative therapies for beta-thalassemia major | Semantic Scholar
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Pediatric Thalassemia: Practice Essentials, Background, Pathophysiology
PDF) Cure for thalassemia major – From allogeneic hematopoietic stem cell transplantation to gene therapy
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Introductory Chapter: β-Thalassemia | IntechOpen
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia
Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases
Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article - Cureus
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis