Esclusione semaforo Nuvoloso cappellini and thalassemia treatments haematologica 2017 sciopero Faringe Occidentale

Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia

Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells

Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects

Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)

JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?

Plasma proteome profiling combined with clinical and genetic features reveals the pathophysiological characteristics of β-thalassemia - ScienceDirect

Guidelines for the Management of Non-Transfusion Dependent Thalassaemias (2nd edition - 2017) by Thalassaemia International Federation (TIF) - Issuu

Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica

Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases

Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review

PDF) Cure for thalassemia major – From allogeneic hematopoietic stem cell transplantation to gene therapy

Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library

IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?

Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy

Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health

Pediatric Thalassemia: Practice Essentials, Background, Pathophysiology

Β-Thalassemias | NEJM

Β-Thalassemias | NEJM

IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis

Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)

Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis

Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia

Thalassaemia - The Lancet

β-Thalassemia | Genetics in Medicine

PDF] Current and future alternative therapies for beta-thalassemia major | Semantic Scholar

Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink